A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Muscular Dystrophy Association family members and Burn Boot Camp leadership are making a difference kicking off the 9th annual ‘Be Their Muscle’ campaign. CHARLOTTE, N.C., March 31 ...

A young person with Duchenne muscular dystrophy died following treatment with the recently approved gene therapy ...

HONOLULU (KHON2) — Rachel Kondo, creator and head writer of the hit series Shogun, has never shied away from confronting life’s most difficult challenges. Growing up on the island of Maui ...

Wave Life Sciences’ experimental treatment for Duchenne muscular dystrophy hit the mark in a mid-stage study, setting the stage for a new therapeutic option for patients with the rare disease.

WASHINGTON (AP) — Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.

About Duchenne Muscular Dystrophy DMD is a progressive neuromuscular disorder caused by a mutation in the DMD gene which affects the production of a protein called dystrophin. 3 Dystrophin is a ...

demonstrated clinically meaningful and statistically significant improvements across key measures of motor function in boys with Duchenne muscular dystrophy (DMD) Muscle pathology as measured by ...

CHARLOTTE, N.C., March 31, 2025 (GLOBE NEWSWIRE) -- Muscular Dystrophy Association (MDA) has teamed up with Burn Boot Camp, a leading boutique fitness franchise, for the 9th annual national 'Be ...