Duchenne Muscular Dystrophy: diagnosis, clinical development and global researchMuscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, ...

Just a few weeks after Avidity Biosciences made a stir with new data on its experimental therapy for Duchenne muscular dystrophy ... DMD patients with DMD mutations amenable to exon 44 skipping ...

Genomics Market Liquid Biopsy Liquid biopsy is a non-invasive method for detecting cancer by analyzing blood samples for genetic mutations ...

Italfarmaco’s oral HDAC inhibitor givinostat has been approved in the US as a treatment for Duchenne muscular dystrophy ... specifically target genetic mutations like Sarepta Therapeutics ...

New Gene Therapy for Muscular Dystrophy Offers Hope July 17 ... a specific form of inherited deafness called DFNA50 caused by mutations in microRNA, by using a novel in vivo CRISPR genome editing ...

for people living with Duchenne muscular dystrophy mutations a We recently compiled a list of the 12 Best Multibagger Stocks to Buy Right Now. In this article, we are going to take a look at where ...

Grey’s Anatomy” and “Euphoria” star Eric Dane has revealed his ALS diagnosis, a progressive neurodegenerative condition that ...

Health Canada granted priority review to an application seeking approval of vamorolone, marketed in the U.S. as Agamree, for ...

Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.

Eric Dane, best known for his role as the charismatic Dr. Mark Sloan—aka McSteamy—on Grey's Anatomy, has revealed that he has been diagnosed with amyotrophic lateral sclerosis (ALS) ...