Forbes Advocate10d
Local young warrior sparks awareness for Rare Disease Day
On Friday, 14 March 14, IDFA CEO Carolyn Dews and Emma Baxter, mother of local young warrior Jack Baxter, will visit the ...
The Manila Times15d
Can-Fite to Initiate Phase II Study in the Rare Genetic Disease Lowe Syndrome with Piclidenoson
FDA & EMA approvals for rare genetic diseases are fast and require clinical studies with small number of patients. Ramat Gan, Israel, March 19, 2025 (GLOBE NEWSWIRE) -- Can-Fite B ...
Nasdaq15d
Can-Fite BioPharma Initiates Phase II Clinical Study for Piclidenoson in Patients with Lowe Syndrome
This therapeutic approach is in an advanced stage of development for another immunodeficiency, Wiskott-Aldrich syndrome. Other diseases on which the gene therapy developed by Telethon researchers ...
Morningstar15d
Can-Fite to Initiate Phase II Study in the Rare Genetic Disease Lowe Syndrome with Piclidenoson
This therapeutic approach is in an advanced stage of development for another immunodeficiency, Wiskott-Aldrich syndrome. Other diseases on which the gene therapy developed by Telethon researchers ...
Medical News Today3d
The function of lymphocytes and healthy levels
In some cases, people can inherit lymphocytopenia. For example, people with Wiskott-Aldrich syndrome have genetic mutations that reduce the body’s capacity to produce lymphocytes. Doctors will ...
Hosted on MSN25d
Any Baby Can hosts annual Butterfly Memorial to honor children lost by grieving families
Their first son, Miles, diagnosed with Wiskott-Aldrich syndrome at age two, passed away in 2021 at the age of four. Tragically, their second son, Aidan, also diagnosed with the same syndrome ...
rarediseaseadvisor9d
Early Diagnosis of WAS Reduces Delays in Life-Saving Treatment
Misdiagnosis of FNAIT can delay critical interventions for congenital disorders such as Wiskott-Aldrich syndrome. Fetal and neonatal alloimmune thrombocytopenia (FNAIT) is frequently suspected in ...