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Jeff Erlanger was a longtime fan of Fred Rogers before appearing on his show, and the two became friends for life ...
Muscular Dystrophy Association family members and Burn Boot Camp leadership are making a difference kicking off the 9th annual ‘Be Their Muscle’ campaign. CHARLOTTE, N.C., March 31 ...
Kye Pharmaceuticals, Inc. ("Kye") announced today it has submitted a New Drug Submission (NDS) to Health Canada for the ...
A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short, but researchers say the lessons learned could pave the way for better, more effective treatments.
A national-level workshop on muscular dystrophy and related genetic disorders was held at the Integrated Muscular Dystrophy Rehabilitation Centre (IMDRC), Manav Mandir, in Kothon village.
SAN DIEGO — Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory boys with Duchenne muscular dystrophy, interim data show.
A recent discovery of a molecular connection between autism and myotonic dystrophy, a type of neuromuscular disease, may provide a breakthrough on how clinicians approach autism spectrum disorder.
CHARLOTTE, N.C., March 31, 2025 (GLOBE NEWSWIRE) -- Muscular Dystrophy Association (MDA) has teamed up with Burn Boot Camp, a leading boutique fitness franchise, for the 9th annual national 'Be ...
More information: Dariusz C. Górecki et al, Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy (2025). DOI: 10.1038/s41434-025-00531-y ...
“There are no disease-modifying treatments approved for patients with any subtype of limb-girdle muscular dystrophy, and the unmet medical need is significant. Following feedback from U.S ...
Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...