When her son reached three last year, a new name loomed over their lives — Duchenne Muscular Dystrophy (DMD), a muscle ... Jantar Mantar echoed in unison: to the slogan of "Save our sons!" ...

A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular ...

A national-level workshop on muscular dystrophy and related genetic disorders was held at the Integrated Muscular Dystrophy Rehabilitation Centre (IMDRC), Manav Mandir, in Kothon village.

SAN DIEGO — Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory boys with Duchenne muscular dystrophy, interim data show.

A local gas station, likely with a location near you, has successfully raised over $41,000 for the Muscular Dystrophy ...

Throughout the period of February 3 to March 16, the team at Cliff’s Local Market led their annual fundraising campaign in aid of the Muscular Dystrophy Association raising $41,515.

Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy , 2025; DOI: 10.1038/s41434-025-00531-y Cite This Page : ...

More information: Dariusz C. Górecki et al, Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy (2025). DOI: 10.1038/s41434-025-00531-y ...

This is the ninth year MDA has teamed up with the Blaine studio to raise funds to help those with neuromuscular diseases live ...

Upon approval, vamorolone would be the first and only treatment option indicated for patients diagnosed with Duchenne muscular dystrophy in Canada The Canadian regulatory submission of vamorolone ...

Colton Belluzzo was diagnosed with a form of muscular dystrophy when he was a baby. The disease has weakened his muscles over time. But he and his family now have good reason to be optimistic.

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...